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Cell & Gene: The Podcast
Cell & Gene: The Podcast

Why In Vivo Therapies Are Moving Toward the Clinic with Ascidian Therapeutics' Dr. Mike Ehlers

Jun 12, 2026 · 18m
✨ AI Summary
  • Dr. Mike Ehlers discusses Ascidian Therapeutics' RNA exon editing for genetic diseases.
  • Focus on durably correcting disease at the transcript level without DNA alteration.
  • In vivo therapies must prove precision, durability, and predictability in clinic.

Guests on This Episode

ME
Mike Ehlers
1 podcast appearance

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